JCR Pharmaceuticals’ unique brain-shuttling technology opens new treatment opportunities for meeting the needs of patients grappling with CNS diseases. Getting drugs from the bloodstream into the ...
Please provide your email address to receive an email when new articles are posted on . Meaningful progress is being made in the development of gene therapies for rare neurological diseases caused by ...
Neurogene, formed from multiple mergers, has a $903M market cap with two phase 1/2 assets, NGN-401 for Rett Syndrome and NGN-101 for CLN5 Batten Disease. NGN-401, an AAV9 gene therapy for Rett ...
Experiments on an ultra-rare genetic mutation that causes neurodegeneration in children have helped uncover a new mechanism ...
Oral bacteria that migrate to the gut can generate metabolites that reach the brain and accelerate Parkinson’s disease.
MOG antibody-associated disease (MOGAD) is a rare autoimmune disease of the central nervous system. The blood of patients ...
Scientists said a novel compound can arrest early stages of Alzheimer's disease in mice brains, setting the stage for a ...
The ability to follow patients with this high sensitivity allows us to make a more accurate and precise measurement, and we can see small changes or see them in a shorter period of time…,” ...
For over a century, Alzheimer's disease (AD) has been considered irreversible. Consequently, research has focused on disease ...
A girl diagnosed with a rare brain disease after suddenly becoming unresponsive at home has been "fighting like hell", her ...