Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...
Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of SYNGAP1-related disorder, a devastating condition affecting an estimated 1 million ...
Scientists have reversed diabetic heart failure with a genetic therapy in mice and miniature human "hearts" grown from stem ...
In May, a historic moment in science and medicine was captured in a single photo that circulated across news outlets ...
MIT scientists have found a way to make gene editing far safer and more accurate — a breakthrough that could reshape how we treat hundreds of genetic diseases. By fine-tuning the tiny molecular “tools ...
Bayer agreed to acquire unlisted U.S. biotech firm Asklepios BioPharmaceutical Inc for as much as $4 billion in a bet on gene therapy with the help of modified viruses.
Smarter design through targeted delivery and human-relevant testing can save the industry from costly safety failures.
As industry leaders gather at the annual event in Phoenix, the cell and gene therapy space remains in a state of flux, with M ...