While columnist Alyssa Silva has a lot of experience with certain health procedures, that doesn't make them easier to ...

Novartis has confirmed that at least two reports of tumors appear to have been caused by treatment with the gene therapy ...

SMA treatment with Spinraza was linked to early motor improvements and long-term stability in people with SMA types 2 and 3, ...

I hadn’t even used AI for research until a couple months ago. Moreover, the ease with which you could generate 50,000 words ...

Spinraza improved motor function in children and adolescents with SMA in a real-world study from Czechia and Slovakia.

As part of his ongoing efforts to encourage others, columnist Ari Anderson shares his plans to write a book about his life ...

Two interconnected themes — community and hope — dominated conversations at this year's MDA Engage symposium in Dallas.

Columnist Halsey Blocher was impressed by the accessibility and inclusivity she encountered in a small Bavarian town in ...

Canada’s Drug Agency recommends expanding public funding for Biogen’s Spinraza to include adults and more patients with SMA.

Spinal muscular atrophy (SMA) type 1, also called infantile-onset SMA or Werdnig-Hoffmann disease, is the most common form of SMA and can lead to muscle weakness and difficulties with breathing, ...

Type 3 is a milder form of spinal muscular atrophy (SMA), a rare genetic disease that results in muscle weakness and wasting. One of five main forms of the disease, type 3 is sometimes called juvenile ...