Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of SYNGAP1-related disorder, a devastating condition affecting an estimated 1 million ...

MIT scientists have found a way to make gene editing far safer and more accurate — a breakthrough that could reshape how we ...

Bayer AG has struck a deal with Atara Biotherapeutics to jointly work on Atara's CAR-T cell anti-tumour treatments, as the German group firms up its commitment to build a specialist cell and gene ...

Bayer agreed to acquire unlisted U.S. biotech firm Asklepios BioPharmaceutical Inc for as much as $4 billion in a bet on gene therapy with the help of modified viruses.

Scientists have discovered that mutations in the EPG5 gene—known for causing the rare childhood disorder Vici syndrome—also increase the risk of Parkinson’s disease and dementia later in life.

Errors in a gene known to cause a serious neurodevelopmental condition in infants are also linked to the development of Parkinson's disease in adolescence and adulthood, according to new research.

Here is our Top Docs 2025 profile on Dana Zakalik, M.D., who is a geneticist and obstetrician at Corewell Health.

In May, a historic moment in science and medicine was captured in a single photo that circulated across news outlets ...

Errors in a gene known to cause a serious neurodevelopmental condition in infants are also linked to the development of Parkinson's disease in adolescence and adulthood, according to new research.

Each year I like to write a post about the Nobel Prize in Physiology or Medicine. While advocating for higher standards of science in medicine we tend to spend much of our time criticizing pseudoscie ...

HIRI and liver transplantation animal models, primary cell co-cultures and adeno-associated virus-mediated gene knockdown were used to prove cellular function and mechanisms. Neutralising antibody was ...